This campaign has now closed
We are seeking to further fund Sutura Therapeutics groundbreaking research to radically enhance the delivery and efficacy of RNA-targeting antisense oligonucleotide-based genetic medicines for Duchenne. Dr Keith Foster's work is showing promising results that we want to continue to support
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Beneficiaries
Situation
Duchenne Muscular Dystrophy is a fatal genetic condition which children are born with. It affects approximately 1 in 3,500 live male births and there are currently around 2,500 children and young people living with Duchenne in the UK. Duchenne causes muscles to waste away over time because the body does not produce dystrophin, the protein required to strengthen, grow and repair muscles. The life expectancy is currently just 25 years. Our aim is to fund the world's best research to find a cure.
Solution
By funding promising and groundbreaking research, we seek to find treatments that are effective for all people living with Duchenne. Currently, any available treatments are problematic with unwanted side effects and are only able to help approximately 13% of those with the condition. Research work by Dr Keith Foster is showing positive results in reaching all muscles in the body, including the heart, which has been a stumbling block for many other researchers.